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3D-stem cell spinal cord model: a new tool to study risdiplam mechanisms and therapeutic effects for Spinal Muscular Atrophy

Project
Ricerca pre-clinica incentrata sullo studio, tramite un modello 3Dstem cell spinal cord, del meccanismo d’azione e degli effetti terapeutici delle molecole SMN2 splicing modifier.
  • Overview
  • Research Areas

Overview

Contributors

CORTI STEFANIA PAOLA   Scientific Manager  

Departments involved

Dipartimento di Fisiopatologia Medico-Chirurgica e dei Trapianti   Principale  

Type

CONTR_ASPR - Contratti di ricerca finanziata da associazioni e altri soggetti privati

Funder

ROCHE S.P.A.
External Organization Funding Organization

Date/time interval

September 1, 2020 - January 31, 2022

Project duration

17 months

Research Areas

Concepts


Settore MED/26 - Neurologia
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